Innovative Gene Therapy Article Review https://www.pharmacytimes

What is the main genetic disorder discussed in the article?

• Cystic fibrosis

• Sickle cell anemia

• Hemophilia

• Thalassemia

Which type of therapy was used to cure the patient in the article?

• Chemotherapy

• Gene therapy

• Radiation therapy

• Immunotherapy

What is the primary cause of sickle cell anemia?

• Bacterial infection

• Genetic mutation

• Vitamin deficiency

• Autoimmune response

Which cell type is primarily affected in sickle cell anemia?

• White blood cells

• Platelets

• Red blood cells

• Nerve cells

What is the main goal of gene therapy in treating sickle cell anemia?

• To kill cancer cells

• To correct the faulty gene causing the disease

• To boost the immune system

• To reduce cholesterol levels

Which of the following best describes gene therapy?

• Using drugs to treat symptoms

• Modifying or replacing faulty genes to treat disease

• Removing organs to stop disease

• Using physical therapy to improve health

What is a common symptom of sickle cell anemia?

• High blood pressure

• Joint pain

• Frequent urination

• Hair loss

Which innovative technique was used to modify the patient’s genes in the case study?

• CRISPR-Cas9

• Bone marrow transplant

• Antibiotic therapy

• Chemotherapy

How does sickle cell anemia affect the shape of red blood cells?

• They become rounder

• They become sickle-shaped

• They become larger

• They become square-shaped

Why is gene therapy considered an innovative treatment for sickle cell anemia?

• It uses traditional medications

• It targets the root genetic cause of the disease

• It only treats symptoms

• It is less expensive than other treatments