Changing DNA in a Cell With No DNA: Gene Therapy for Blood Disorders

The video discusses gene therapy's potential to treat genetic diseases, focusing on sickle cell disease. It explains the challenges and advancements in gene therapy, including the use of lentivirus and gene editing techniques. The video also explores the reactivation of gamma-globin as a promising treatment for sickle cell and other blood disorders. Despite the challenges, ongoing research offers hope for effective treatments.

What are the potential risks associated with using modified viruses in gene therapy?

Discuss the future prospects of gene therapy for blood disorders based on current research.

How have researchers learned from the challenges of developing treatments for sickle cell disease?