Gene Therapy Concepts and Ethics

The video discusses gene therapy, a biotechnology method for treating diseases by altering DNA. It explains various mechanisms, such as gene editing and vectors, and highlights historical milestones. The impact of gene therapy on medicine, ethical concerns, and its future potential are also explored.

What is the primary goal of gene therapy?

• To enhance physical traits

• To change a person's DNA to treat diseases

• To create new genetic disorders

• To eliminate all genetic variations

Which of the following is NOT a method used in gene therapy?

• Replacing a faulty gene with a healthy one

• Creating new genetic disorders

• Inactivating a disease-causing gene

• Adding new genes to the body

What is a vector in the context of gene therapy?

• A protein that repairs damaged cells

• A type of virus that causes diseases

• A genetically engineered vehicle to deliver genes

• A molecule that breaks down DNA

Which vector is commonly used in ex vivo gene therapy?

• Adeno-associated viral vectors

• Lentiviral vectors

• Retroviral vectors

• Bacterial plasmids

When was gene therapy first officially administered to humans?

• 1990

• 1970

• 1961

• 1980

Which company authorized the first gene therapy in the U.S.?

• Johnson & Johnson

• Novartis

• Merck

• Pfizer

What percentage of people in a 2001 survey hoped for genetic research to cure serious diseases?

• 54%

• 95%

• 70%

• 88%

What is a major ethical concern regarding gene therapy?

• It has no potential for misuse

• It is too easy to implement

• It could be used to enhance basic human traits

• It may lead to the extinction of certain species

What is the estimated increase in spending due to gene therapy from 2020 to 2034?

• 20.1%

• 15.7%

• 12.3%

• 10.5%

Which diseases are mentioned as potential targets for gene therapy?

• Cystic fibrosis and cancer

• Common cold and flu

• Arthritis and osteoporosis

• Allergies and asthma