Batten Disease and Gene Therapy Quiz

What is Batten disease primarily characterized by?

• A type of cancer

• A bacterial infection

• A group of rare genetic disorders affecting the nervous system

• A common viral infection

What is the primary function of lysosomes in cells?

• To produce energy

• To break down and remove waste

• To store genetic information

• To transport nutrients

Which treatment is currently available for only one form of Batten disease?

• Radiation therapy

• Chemotherapy

• Enzyme replacement therapy

• Gene therapy

How does gene therapy aim to treat Batten disease?

• By removing faulty genes

• By introducing working genes to produce necessary proteins

• By using antibiotics

• By increasing the number of lysosomes

What is used as a vector to deliver therapeutic genes in gene therapy?

• Bacteria

• Fungi

• Parasites

• Viruses