FDA Advisers Reviewed a Sickle Cell Treatment

The video discusses sickle cell anemia, highlighting the severe pain and challenges faced by patients. It explains the genetic mutation causing the disease and current treatments like bone marrow transplants. A new gene-editing drug, Exa Cell, is under FDA review, potentially offering a breakthrough treatment. However, concerns about safety and research limitations are noted. The FDA's decision is expected soon, with researchers planning long-term patient monitoring.

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