Limb Girdle Muscular Dystrophy Quiz

What muscles are primarily affected by limb girdle muscular dystrophy?

• Abdominal muscles

• Facial muscles

• Shoulders, upper arms, hips, and thighs

• Hands and feet

How does a recessive gene mutation affect protein production in LGMD?

• It produces excess proteins

• It results in no functional protein being produced

• It causes proteins to be produced in the wrong location

• It enhances protein function

What is the role of vectors in gene therapy for LGMD?

• To enhance muscle strength directly

• To deliver therapeutic genes into cells

• To diagnose genetic mutations

• To remove faulty genes

What is the primary goal of antisense therapy in treating LGMD?

• To enhance the immune response

• To increase the production of faulty proteins

• To replace muscle tissue

• To block the production of faulty proteins

What is the main focus of ongoing research and clinical trials for LGMD?

• Finding a cure for all genetic diseases

• Creating new diagnostic tools

• Developing new surgical techniques

• Ensuring gene therapies are safe and effective